3621. PAM-flexible adenine base editing rescues hearing loss in a humanized MPZL2 mouse model harboring an East Asian founder mutation
Hu SW, Jeong S, Jiang L, Koo H, Wang Z, Choi WH, Zhu B, Seok H, Zhou Y, Kim MG, Mu D, Guo H, Zhou Z, Jung SH, Zhang Y, Chae HB, Chen L, Lee SY, Guo L, Suh MW, Xiao Y, Park MK, Tang H, Song JJ, Chen X, Chen A, Lee JH, Bae S, Lee SY, Shu Y.
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